GMS 6059:  Gene Therapy from Bench to Bedside


Catalog description:  This course will cover the design and use of gene transfer vectors for treating a variety of diseases and will provide a practical understanding of the successes and hurdles that are faced in gene therapy today with topics that are current.



Prerequisites/corequisites:  GMS 6034, GMS 6035 and GMS 6036, or permission of instructor.

Expanded description and explanation:  


Evaluation of student performance:   


Faculty:  Dr. Richard Snyder will be the course director. He will be assisted by faculty from the College of Medicine who are experts in human genetics.


Summary of Topics: 

Introductory Lecture and Viral vectors
Lecture # 1:  Vectors: Viral and Non-Viral
Student review of 2 Papers 
Lecture # 2:  Gene Transfer Experiment Design
Student review of 2 Papers
Lecture # 3:  Control of Vector Gene Expression
Student review of 2 Papers
Lecture # 4:  Gene Therapy Applications : Cardiovascular
Student review of 2 Papers
Lecture # 5:  Gene Therapy Applications : Inherited Monogenic Diseases
Student review of 2 Papers
Lecture # 6:  Gene Theapy Applications : CNS
Student review of 2 Papers
Lecture # 7:  Gene Transfer Experiments : Clinical
Student review of 2 Papers


Assigned readings:  Reading assignments will included pertinent review articles and original papers assigned by the faculty.


5-5-03 WTM